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Navigating the Complex Market Landscape of Rare Genetic Disorders: A Deep Dive into Hereditary Angioedema, Wilson Disease, Menkes Disease, and Alpha-1 Antitrypsin Deficiency (AATD) | DelveInsight
www.ultragenyx.com Transforming good science into great medicine for rare genetic diseases February 17, 2022 Dear Members and Fr
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Ultragenyx announces US FDA has granted orphan drug designation to UX701 for the treatment of Wilson Disease
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